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Searching for hope while living with a rare disease

Published on: February 21, 2020
Last updated: September 23, 2022

Isabella is in the early stages of a clinical trial for a drug intended to treat a rare pediatric disease called Mucopolysaccharidosis IIIA.

Link: https://health.choc.org/searching-for-hope-while-living-with-a-rare-disease/